نتایج جستجو برای: griscelli syndrome

تعداد نتایج: 621919  

2015
Guoqiang Zhang Yuping Lin Xianni Qi Lixian Wang Peng He Qinhong Wang Yanhe Ma

BACKGROUND Sugar alcohols have been widely applied in the fields of food and medicine owing to their unique properties. Compared to chemical production, microbial production of sugar alcohols has become attractive because of its environmentally friendly and sustainable characteristics. Our previous study identified the nonconventional yeast Pichia anomala TIB-x229 as a potential producer of sug...

2008
A. Salmi P. C. de Vries

Experiments have been carried out in the JET tokamak in order to determine the critical ion temperature inverse gradient length (R/LTi =R|!Ti|/Ti) for the onset of Ion Temperature Gradient modes and the stiffness of Ti profiles with respect to deviations from the critical value. The existence of a threshold in R/LTi has been assessed and its value found in close agreement with linear GS2 gyro-k...

2016
S. L. W. On B. L. Siemer S. M. Brandt A. J. Lastovica

Amplified Fragment Length Polymorphism (AFLP) profiling was used to evaluate the distribution of phenotypically indistinguishable, but genetically distinct, among Campylobacter concisus strains from South Africa. A Polymerase Chain Reaction (PCR) assay described for identifying strains belonging to Genomospecies 1 and 2 was applied in this study. Forty-seven C. concisus strains were studied in ...

Journal: :Blood 2009
Jana Pachlopnik Schmid Despina Moshous Nathalie Boddaert Bénédicte Neven Liliane Dal Cortivo Marc Tardieu Marina Cavazzana-Calvo Stéphane Blanche Geneviève de Saint Basile Alain Fischer

Allogeneic hematopoietic stem cell transplantation (HSCT) is the only curative treatment for Griscelli syndrome type 2, an inherited immune disorder causing fatal hemophagocytic lymphohistiocytosis (HLH). Optimal therapeutic modalities are not yet well known. We retrospectively analyzed the outcome for 10 patients who underwent HSCT in a single center between 1996 and 2008. Seven patients (70%)...

Journal: :Blood 2013
Birthe Jessen Sebastian F N Bode Sandra Ammann Subarna Chakravorty Graham Davies Jana Diestelhorst Melissa Frei-Jones William A Gahl Bernadette R Gochuico Matthias Griese Gillian Griffiths Gritta Janka Christoph Klein Tamara Kögl Karin Kurnik Kai Lehmberg Andrea Maul-Pavicic Andrew D Mumford David Pace Nima Parvaneh Nima Rezaei Geneviève de Saint Basile Annette Schmitt-Graeff Klaus Schwarz Gulsun T Karasu Barbara Zieger Udo Zur Stadt Peter Aichele Stephan Ehl

Genetic disorders of lymphocyte cytotoxicity predispose patients to hemophagocytic lymphohistiocytosis (HLH). Reduced lymphocyte cytotoxicity has been demonstrated in Hermansky-Pudlak syndrome type 2 (HPS2), but only a single patient was reported who developed HLH. Because that patient also carried a potentially contributing heterozygous RAB27A mutation, the risk for HLH in HPS2 remains unclear...

2006
Anselm Enders Barbara Zieger Klaus Schwarz Ayami Yoshimi Carsten Speckmann Eva-Maria Knoepfle Udo Kontny Christoph Müller Alan Nurden Jan Rohr Matthias Henschen Ulrich Pannicke Charlotte Niemeyer Paquita Nurden Stephan Ehl

Griscelli syndrome (GS) was diagnosed in a 2-year-old patient with oculocutaneous albinism and immunodeficiency, but sequencing of RAB27a revealed only a heterozygous mutation. Due to impaired natural killer (NK) and T-cell cytotoxicity implying a high risk of developing hemophagocytic lymphohistiocytosis (HLH), he was prepared for hematopoietic stem cell transplantation (HSCT). Unexpectedly, a...

Journal: :Blood 2012
Yenan T Bryceson Daniela Pende Andrea Maul-Pavicic Kimberly C Gilmour Heike Ufheil Thomas Vraetz Samuel C Chiang Stefania Marcenaro Raffaella Meazza Ilka Bondzio Denise Walshe Gritta Janka Kai Lehmberg Karin Beutel Udo zur Stadt Nadine Binder Maurizio Arico Lorenzo Moretta Jan-Inge Henter Stephan Ehl

Familial hemophagocytic lymphohistiocytosis (FHL) is a life-threatening disorder of immune regulation caused by defects in lymphocyte cytotoxicity. Rapid differentiation of primary, genetic forms from secondary forms of hemophagocytic lymphohistiocytosis (HLH) is crucial for treatment decisions. We prospectively evaluated the performance of degranulation assays based on surface up-regulation of...

Journal: :Pediatric transplantation 2013
Amir Ali Hamidieh Zahra Pourpak Kolsoum Yari Mohammad Reza Fazlollahi Susan Hashemi Maryam Behfar Mostafa Moin Ardeshir Ghavamzadeh

Partial albinism with variable immunodeficiency are the two major characteristics of Griscelli syndrome type 2 (GS-2). This syndrome is usually associated with a high mortality rate and commonly results in early childhood death. Patients suffer from different infections and experience crisis of HLH. HSCT remains the sole curative treatment for GS-2. We prospectively analyzed the outcomes of tra...

Journal: :The Journal of Cell Biology 2001
Alistair N. Hume Lucy M. Collinson Andrzej Rapak Anita Q. Gomes Colin R. Hopkins Miguel C. Seabra

Rab GTPases are regulators of intracellular membrane traffic. We report a possible function of Rab27a, a protein implicated in several diseases, including Griscelli syndrome, choroideremia, and the Hermansky-Pudlak syndrome mouse model, gunmetal. We studied endogenous Rab27a and overexpressed enhanced GFP-Rab27a fusion protein in several cultured melanocyte and melanoma-derived cell lines. In p...

Journal: :Dermatology 2009
Alfredo Rossi Riccardo G Borroni Anna Maria Carrozzo Catia de Felice Adriana Menichelli Marta Carlesimo Stefano Calvieri

Griscelli syndrome (GS) is a rare autosomal recessive disease characterized by silvery hair ('partial albinism'). Three forms exist; GS type 2 (GS2), the most common one, is characterized by severe primary immunodeficiency with acute episodes of hemophagocytic lymphohistiocytosis (HLH) which may be fatal in the absence of hematopoietic stem cell transplantation. A 5-year-old boy with HLH was re...

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