نتایج جستجو برای: npc2

تعداد نتایج: 199  

2009
Stefania Zampieri Synthia H Mellon Terry D Butters Marco Nevyjel Douglas F Covey Bruno Bembi Andrea Dardis

Niemann-Pick C disease (NPC) is an autosomal recessive neurodegenerative disorder caused by the abnormal function of NPC1 or NPC2 proteins, leading to an accumulation of unesterified cholesterol and glycosphingolipids (GSLs) in the lysosomes. The mechanisms underlying the pathophysiology in NPC disease are not clear. Oxidative damage is implicated in the pathophysiology of different neurologica...

2014
Sara Wouters Linda De Meirleir Edward Campforts Annik Lampo

Niemann-Pick disease type C (NP-C) is a rare autosomal-recessively inherited lysosomal storage disorder. It is caused by mutations in the NPC1 (95%) or NPC2 gene. It is a progressive and highly heterogeneous disease, characterized by the presentation of visceral, neurological, and psychiatric symptoms. Apart from the patients that die early from organic failure, most of the patients with juveni...

Journal: :Development 2005
Xun Huang Kaye Suyama Joann Buchanan Alan J Zhu Matthew P Scott

Niemann-Pick type C (NPC) disease is a fatal autosomal-recessive neurodegenerative disorder characterized by the inappropriate accumulation of unesterified cholesterol in aberrant organelles. The disease is due to mutations in either of two genes, NPC1, which encodes a transmembrane protein related to the Hedgehog receptor Patched, and NPC2, which encodes a secreted cholesterol-binding protein....

Journal: :Blood 2014
Anneliese O Speak Danielle Te Vruchte Lianne C Davis Anthony J Morgan David A Smith Nicole M Yanjanin Louise Simmons Ralf Hartung Heiko Runz Eugen Mengel Michael Beck Jackie Imrie Elizabeth Jacklin James E Wraith Christian Hendriksz Robin Lachmann Celine Cognet Rohini Sidhu Hideji Fujiwara Daniel S Ory Antony Galione Forbes D Porter Eric Vivier Frances M Platt

Niemann-Pick type C (NPC) is a neurodegenerative lysosomal storage disorder caused by defects in the lysosomal proteins NPC1 or NPC2. NPC cells are characterized by reduced lysosomal calcium levels and impaired sphingosine transport from lysosomes. Natural killer (NK) cells kill virally infected/transformed cells via degranulation of lysosome-related organelles. Their trafficking from lymphoid ...

Journal: :Biochemical Society transactions 2006
J E Vance B Karten H Hayashi

Compared with other organs, the brain is highly enriched in cholesterol. Essentially all cholesterol in the brain is synthesized within the brain; the blood-brain barrier prevents the import of plasma lipoproteins into the brain. Consequently, the brain operates an independent lipoprotein transport system in which glial cells produce ApoE (apolipoprotein E)-containing lipoproteins that are thou...

Journal: :Arteriosclerosis, thrombosis, and vascular biology 2008
Stephanie Bultel Lionel Helin Veronique Clavey Giulia Chinetti-Gbaguidi Elena Rigamonti Morvane Colin Jean-Charles Fruchart Bart Staels Sophie Lestavel

OBJECTIVE Liver X receptors (LXRs) are oxysterol-activated nuclear receptors regulating reverse cholesterol transport, in part by modulating cholesterol efflux from macrophages to apoAI and HDL via the ABCA1 and ABCG1/ABCG4 pathways. Moreover, LXR activation increases intracellular cholesterol trafficking via the induction of NPC1 and NPC2 expression. However, implication of LXRs in the selecti...

2012
Mark Walterfang Yin-Hsiu Chien Jackie Imrie Derren Rushton Danielle Schubiger Marc C Patterson

Niemann-Pick disease type C (NP-C) is a rare neurovisceral disease characterised by progressive neurological deterioration and premature death, and has an estimated birth incidence of 1:120,000. Mutations in the NPC1 gene (in 95% of cases) and the NPC2 gene (in approximately 4% of cases) give rise to impaired intracellular lipid metabolism in a number of tissues, including the brain. Typical ne...

2016
André R. A. Marques Tanit L. Gabriel Jan Aten Cindy P. A. A. van Roomen Roelof Ottenhoff Nike Claessen Pilar Alfonso Pilar Irún Pilar Giraldo Johannes M. F. G. Aerts Marco van Eijk Andrea Dardis

Impaired function of NPC1 or NPC2 lysosomal proteins leads to the intracellular accumulation of unesterified cholesterol, the primary defect underlying Niemann-Pick type C (NPC) disease. In addition, glycosphingolipids (GSLs) accumulate in lysosomes as well. Intralysosomal lipid accumulation triggers the activation of a set of genes, including potential biomarkers. Transcript levels of Gpnmb ha...

2014
Hong Zhao Chuan Xu Hsiao-Ling Lu Xiaoxuan Chen Raymond J. St. Leger Weiguo Fang

Metarhizium robertsii is a plant root colonizing fungus that is also an insect pathogen. Its entomopathogenicity is a characteristic that was acquired during evolution from a plant endophyte ancestor. This transition provides a novel perspective on how new functional mechanisms important for host switching and virulence have evolved. From a random T-DNA insertion library, we obtained a pathogen...

2010
Qingyu Qin Guanghong Liao Michel Baudry Xiaoning Bi

Perturbation of lipid metabolism, especially of cholesterol homeostasis, can be catastrophic to mammalian brain, as it has the highest level of cholesterol in the body. This notion is best illustrated by the severe progressive neurodegeneration in Niemann-Pick Type C (NPC) disease, one of the lysosomal storage diseases, caused by mutations in the NPC1 or NPC2 gene. In this study, we found that ...

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