نتایج جستجو برای: type 1 tyrosinemia

تعداد نتایج: 3647237  

2017
Willem G. van Ginkel Danique van Vliet Johannes G. M. Burgerhof Pim de Blaauw M. Estela Rubio Gozalbo M. Rebecca Heiner-Fokkema Francjan J. van Spronsen

INTRODUCTION Hereditary Tyrosinemia type 1 (HT1) is a rare metabolic disease caused by a defect in the tyrosine degradation pathway. Current treatment consists of 2-(2-nitro-4-trifluoromethylbenoyl)-1,3-cyclohexanedione (NTBC) and a tyrosine and phenylalanine restricted diet. Recently, neuropsychological deficits have been seen in HT1 patients. These deficits are possibly associated with low bl...

Journal: :iranian journal of child neurology 0
mohammad reza alaee associate professor of endocrinology, mofid children hospital,shahid beheshti university of medical sciences (sbmu), tehran, iran

how to cite this article: alaee mr. mucopolysaccharidosis type 1. iran j child neurol autumn 2012; 6:4(suppl. 1):5. pls see  pdf.

Journal: :Proceedings of the National Academy of Sciences of the United States of America 2001
J L Aponte G A Sega L J Hauser M S Dhar C M Withrow D A Carpenter E M Rinchik C T Culiat D K Johnson

Hereditary tyrosinemia type 1 (HT1) is a severe autosomal recessive metabolic disease associated with point mutations in the human fumarylacetoacetate hydrolase (FAH) gene that disrupt tyrosine catabolism. An acute form of HT1 results in death during the first months of life because of hepatic failure, whereas a chronic form leads to gradual development of liver disease often accompanied by ren...

2010
Gabriela Gutierrez-Reyes Maria del Carmen Garcia de Leon Gustavo Varela-Fascinetto Pedro Valencia Ruy Pérez Tamayo Claudia Gonzalez Rosado Blanca Farfan Labonne Norma Morales Rochilin Rosalinda Martinez Garcia Jonathan Aguirre Valadez Gabriela Togno Latour Dana Lau Corona Guillermo Robles Diaz Albert Zlotnik David Kershenobich

BACKGROUND Senescent cells occur in adults with cirrhotic livers independent of the etiology. AIM Investigate the presence rate of cellular senescence and expression of cell cycle check points in livers from children with end stage disease. METHODOLOGY/PRINCIPAL FINDINGS Livers of five children aged three years or less undergoing liver transplantation due to tyrosinemia (n = 1), biliary atr...

Journal: :iranian journal of nursing and midwifery research 0
hamid reza roohafza zahra abdeyazdan parvaneh amini saied pahlavanzadeh pedram shokouh

abstract background: an association of eating disorder with diabetes mellitus may lead to a serious lack of metabolic control, higher mortality and morbidity. there is no recent study conducted in the iranian population about eating disorder and its variants. the aim of the present study is investigation of frequency of disturbed eating behaviors in adolescent girls with type 1 diabetes mellitu...

Journal: :The Journal of biological chemistry 2001
A Bergeron M D'Astous D E Timm R M Tanguay

Hereditary tyrosinemia type 1 (HT1) is an autosomal recessive disease caused by a deficiency of the enzyme involved in the last step of tyrosine degradation, fumarylacetoacetate hydrolase (FAH). Thus far, 34 mutations in the FAH gene have been reported in various HT1 patients. Site-directed mutagenesis of the FAH cDNA was used to investigate the effects of eight missense mutations found in HTI ...

2017
Julia Geppert Chris Stinton Karoline Freeman Hannah Fraser Aileen Clarke Samantha Johnson Paul Sutcliffe Sian Taylor-Phillips

BACKGROUND Tyrosinemia type 1 (TYR1) is a rare autosomal recessive disorder of amino acid metabolism that is fatal without treatment. With medication (nitisinone) and dietary restrictions outcomes are improved. We conducted a systematic review to investigate if treatment with nitisinone following screening provides better long-term outcomes than treatment with nitisinone following symptomatic d...

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