نتایج جستجو برای: friedreichs ataxia frda

تعداد نتایج: 17887  

Journal: :F1000Research 2023

A major cause of death in the elderly worldwide is attributed to neurodegenerative diseases, such as AD (Alzheimer’s disease), PD (Parkinson’s ALS (Amyotrophic lateral sclerosis), FRDA (Friedreich’s ataxia), VaD (Vascular dementia) etc. These can be caused due multiple factors genetic, physiological problems like stroke or tumor, even external causes viruses, toxins, chemicals. T3s (toco...

2015
Michael Lazaropoulos Yina Dong Elisia Clark Nathaniel R Greeley Lauren A Seyer Karlla W Brigatti Carlton Christie Susan L Perlman George R Wilmot Christoper M Gomez Katherine D Mathews Grace Yoon Theresa Zesiewicz Chad Hoyle Sub H Subramony Alicia F Brocht Jennifer M Farmer Robert B Wilson Eric C Deutsch David R Lynch

OBJECTIVE Friedreich ataxia (FRDA) is an autosomal recessive ataxia resulting from mutations in the frataxin gene (FXN). Such mutations, usually expanded guanine-adenine-adenine (GAA) repeats, give rise to decreased levels of frataxin protein in both affected and unaffected tissues. The goal was to understand the relationship of frataxin levels in peripheral tissues to disease status. METHODS...

2016
Maya Patel Charles J. Isaacs Lauren Seyer Karlla Brigatti Sarah Gelbard Cassandra Strawser Debbie Foerster Julianna Shinnick Kimberly Schadt Eppie M. Yiu Martin B. Delatycki Susan Perlman George R. Wilmot Theresa Zesiewicz Katherine Mathews Christopher M. Gomez Grace Yoon Sub H. Subramony Alicia Brocht Jennifer Farmer David R. Lynch

OBJECTIVE Friedreich ataxia (FRDA) is a progressive neurodegenerative disorder of adults and children. This study analyzed neurological outcomes and changes to identify predictors of progression and generate power calculations for clinical trials. METHODS Eight hundred and twelve subjects in a natural history study were evaluated annually across 12 sites using the Friedreich Ataxia Rating Sca...

Journal: :The Journal of biological chemistry 2004
Alexandre A Vetcher Robert D Wells

Our discovery that plasmids containing the Friedreich's ataxia (FRDA) expanded GAA.TTC sequence, which forms sticky DNA, are prone to form dimers compared with monomers in vivo is the basis of an intracellular assay in Escherichia coli for this unusual DNA conformation. Sticky DNA is a single long GAA.GAA.TTC triplex formed in plasmids harboring a pair of long GAA.TTC repeat tracts in the direc...

Journal: :Human molecular genetics 2002
Patrizia Cavadini Heather A O'Neill Oldrich Benada Grazia Isaya

Friedreich ataxia (FRDA) is an autosomal recessive degenerative disease caused by a deficiency of frataxin, a conserved mitochondrial protein of unknown function. Mitochondrial iron accumulation, loss of iron-sulfur cluster-containing enzymes and increased oxidative damage occur in yeast and mouse frataxin-depleted mutants as well as tissues and cell lines from FRDA patients, suggesting that fr...

Journal: :Journal of the neurological sciences 2011
Arnulf H Koeppen

The pathogenic mutation in Friedreich's ataxia (FRDA) is a homozygous guanine-adenine-adenine (GAA) trinucleotide repeat expansion on chromosome 9q13 that causes a transcriptional defect of the frataxin gene. Deficiency of frataxin, a small mitochondrial protein, is responsible for all clinical and morphological manifestations of FRDA. This autosomal recessive disease affects central and periph...

Journal: :Annals of neurology 2011
Giovanni Coppola Ryan Burnett Susan Perlman Revital Versano Fuying Gao Heather Plasterer Myriam Rai Francesco Saccá Alessandro Filla David R Lynch James R Rusche Joel M Gottesfeld Massimo Pandolfo Daniel H Geschwind

OBJECTIVE Gene expression studies in peripheral tissues from patients with neurodegenerative disorders can provide insights into disease pathogenesis, and identify potential biomarkers, an important goal of translational research in neurodegeneration. Friedreich Ataxia (FRDA) is a chronic neurodegenerative disease caused by reduced transcription of frataxin, a ubiquitously expressed protein. We...

Journal: :Human molecular genetics 2008
Stéphane Schmucker Manuela Argentini Nadège Carelle-Calmels Alain Martelli Hélène Puccio

Deficiency in the nuclear-encoded mitochondrial protein frataxin causes Friedreich ataxia (FRDA), a progressive neurodegenerative disorder associating spinocerebellar ataxia and cardiomyopathy. Although the exact function of frataxin is still a matter of debate, it is widely accepted that frataxin is a mitochondrial iron chaperone involved in iron-sulfur cluster and heme biosynthesis. Frataxin ...

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