نتایج جستجو برای: d4z4

تعداد نتایج: 154  

2011
Silvère M. van der Maarel Rabi Tawil Stephen J. Tapscott

Autosomal dominant facioscapulohumeral muscular dystrophy (FSHDI has an unusual pathogenic mecha­ nism. FSHD is caused by deletion of a subset of D4Z4 macrosatellite repeat units in the subtelomere of chro­ mosome 4q. Recent studies provide compelling evi­ dence that a retrotransposed gene in the D4Z4 repeat, DUX4, is expressed in the human germline and then epigenetically silenced in somatie t...

2016
Paul Knopp Yvonne D Krom Christopher R S Banerji Maryna Panamarova Louise A Moyle Bianca den Hamer Silvère M van der Maarel Peter S Zammit

Skeletal muscle wasting in facioscapulohumeral muscular dystrophy (FSHD) results in substantial morbidity. On a disease-permissive chromosome 4qA haplotype, genomic and/or epigenetic changes at the D4Z4 macrosatellite repeat allows transcription of the DUX4 retrogene. Analysing transgenic mice carrying a human D4Z4 genomic locus from an FSHD-affected individual showed that DUX4 was transiently ...

Journal: :genetics in the 3rd millennium 0
bita bozorgmehr mehdi vahid dastjerdi ariana kariminejad

facioscapulohumeral muscular dystrophy (fshd)is characterized by weakness of the facial, scapular muscles  and the dorsiflexors of the foot. severity in this disorder is highly variable. approximately 95% of individuals with fshd phenotype have type 1 fshd, with d4z4 allele of between one and ten repeat units and about 5% have type 2 fshd with mutations in the chromatin modifier smchd1gene whic...

Journal: :Epigenetics 2015
Judit Balog Peter E Thijssen Sean Shadle Kirsten R Straasheijm Patrick J van der Vliet Yvonne D Krom Marlinde L van den Boogaard Annika de Jong Richard J L F Lemmers Rabi Tawil Stephen J Tapscott Silvère M van der Maarel

Facioscapulohumeral muscular dystrophy is caused by incomplete epigenetic repression of the transcription factor DUX4 in skeletal muscle. A copy of DUX4 is located within each unit of the D4Z4 macrosatellite repeat array and its derepression in somatic cells is caused by either repeat array contraction (FSHD1) or by mutations in the chromatin repressor SMCHD1 (FSHD2). While DUX4 expression has ...

Journal: :Human molecular genetics 2013
Natacha Broucqsault Julia Morere Marie-Cécile Gaillard Julie Dumonceaux Julia Torrents Emmanuelle Salort-Campana André Maues De Paula Marc Bartoli Carla Fernandez Anne Laure Chesnais Maxime Ferreboeuf Laure Sarda Henry Dufour Claude Desnuelle Shahram Attarian Nicolas Levy Karine Nguyen Frédérique Magdinier Stéphane Roche

Facio-scapulo-humeral dystrophy (FSHD) results from deletions in the subtelomeric macrosatellite D4Z4 array on the 4q35 region. Upregulation of the DUX4 retrogene from the last D4Z4 repeated unit is thought to underlie FSHD pathophysiology. However, no one knows what triggers muscle defect and when alteration arises. To gain further insights into the molecular mechanisms of the disease, we eval...

Journal: :Human mutation 2015
Francesca Puppo Eugenie Dionnet Marie-Cécile Gaillard Pascaline Gaildrat Christel Castro Catherine Vovan Karine Bertaux Rafaelle Bernard Shahram Attarian Kanako Goto Ichizo Nishino Yukiko Hayashi Frédérique Magdinier Martin Krahn Françoise Helmbacher Marc Bartoli Nicolas Lévy

Facioscapulohumeralmuscular dystrophy (FSHD) is linked to copy-number reduction (N < 10) of the 4q D4Z4 subtelomeric array, in association with DUX4-permissive haplotypes. This main form is indicated as FSHD1. FSHD-like phenotypes may also appear in the absence of D4Z4 copy-number reduction. Variants of the SMCHD1 gene have been reported to associate with D4Z4 hypomethylation in DUX4-compatible...

Journal: :The EMBO journal 2009
Alexandre Ottaviani Caroline Schluth-Bolard Sylvie Rival-Gervier Amina Boussouar Delphine Rondier Andrea M Foerster Julia Morere Serge Bauwens Sophie Gazzo Evelyne Callet-Bauchu Eric Gilson Frédérique Magdinier

The localization of genes within the nuclear space is of paramount importance for proper genome functions. However, very little is known on the cis-acting elements determining subnuclear positioning of chromosome segments. We show here that the D4Z4 human subtelomeric repeat localizes a telomere at the nuclear periphery. This perinuclear activity lies within an 80 bp sequence included within a ...

2015
Eugénie Ansseau Jacqueline S. Domire Lindsay M. Wallace Jocelyn O. Eidahl Susan M. Guckes Carlee R. Giesige Nettie K. Pyne Alexandra Belayew Scott Q. Harper

The DUX4 gene, encoded within D4Z4 repeats on human chromosome 4q35, has recently emerged as a key factor in the pathogenic mechanisms underlying Facioscapulohumeral muscular dystrophy (FSHD). This recognition prompted development of animal models expressing the DUX4 open reading frame (ORF) alone or embedded within D4Z4 repeats. In the first published model, we used adeno-associated viral vect...

2010
Lauren Snider Linda N. Geng Richard J. L. F. Lemmers Michael Kyba Carol B. Ware Angelique M. Nelson Rabi Tawil Galina N. Filippova Silvère M. van der Maarel Stephen J. Tapscott Daniel G. Miller

Each unit of the D4Z4 macrosatellite repeat contains a retrotransposed gene encoding the DUX4 double-homeobox transcription factor. Facioscapulohumeral dystrophy (FSHD) is caused by deletion of a subset of the D4Z4 units in the subtelomeric region of chromosome 4. Although it has been reported that the deletion of D4Z4 units induces the pathological expression of DUX4 mRNA, the association of D...

Journal: :Human molecular genetics 2003
Guanchao Jiang Fan Yang Petra G M van Overveld Vettaikorumakankav Vedanarayanan Silvere van der Maarel Melanie Ehrlich

Facioscapulohumeral muscular dystrophy (FSHD) is a unique dominant disorder involving shortening of an array of tandem 3.3 kb repeats. This copy-number polymorphic repeat, D4Z4, is present in arrays at both 4q35 and 10q26, but only 4q35 arrays with one to 10 copies of the repeat are linked to FSHD. The most popular model for how the 4q35 array-shortening causes FSHD is that it results in a loss...

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