نتایج جستجو برای: neurometabolic disorders

تعداد نتایج: 671446  

Journal: :Seizure 2014
Amira Masri Shourouk Al Wahsh

PURPOSE To examine the characteristics of epilepsy in children with neurometabolic disorders to reveal co morbidities and optimal treatment. METHODS We retrospectively reviewed the files of children diagnosed with a neurometabolic disorder and treated at Jordan University Hospital between 2001 and 2012. We examined the incidence, age at onset, clinical characteristics, and medical control of ...

2013
Katarzyna Krupa Monika Bekiesinska-Figatowska

The purpose of this review is to illustrate the wide spectrum of lesions in the corpus callosum, both congenital and acquired: developmental abnormalities, phakomatoses, neurometabolic disorders, demyelinating diseases, infection and inflammation, vascular lesions, neoplasms, traumatic and iatrogenic injury, and others. Cases include fetuses, children, and adults with rich iconography from the ...

2003
Jayaprakash A. Gosalakkal

Behavioral neurology has been bridging the gap between neurology and psychiatry in children. There are several neuropsychiatric disorders of children in which aggression is a dominant symptom. Both global disorders like attention deficit hyperactivity disorder as well as localized dysfunction of the brain may lead to aggression. A number of neurometabolic disorders as well as post-epileptic and...

Journal: :Annals of neurology 2000
M C Bianchi M Tosetti F Fornai M G Alessandri' P Cipriani G De Vito R Canapicchi

We describe a new creatine metabolism disorder in 2 young sisters who suffered from mental retardation and severe language delay. Blood examination, investigation of the most common neurometabolic disorders, and brain magnetic resonance imaging were normal. Diagnosis was established only by means of in vivo proton magnetic resonance spectroscopy, which disclosed generalized depletion of creatin...

Journal: :Neurology 2013
David Cachia Christy Stine

Organic acidurias are an important group of inherited metabolic disorders that affect the intermediary metabolic pathways of carbohydrate, amino acid, and fatty acid oxidation, leading to the accumulation of organic acids.(1) The 2-hydroxyglutaric acidurias are rare neurometabolic disorders characterized by developmental delay with or without other neurologic dysfunction. Three different subtyp...

Journal: :The New England journal of medicine 2016
Maja Tarailo-Graovac Casper Shyr Colin J Ross Gabriella A Horvath Ramona Salvarinova Xin C Ye Lin-Hua Zhang Amit P Bhavsar Jessica J Y Lee Britt I Drögemöller Mena Abdelsayed Majid Alfadhel Linlea Armstrong Matthias R Baumgartner Patricie Burda Mary B Connolly Jessie Cameron Michelle Demos Tammie Dewan Janis Dionne A Mark Evans Jan M Friedman Ian Garber Suzanne Lewis Jiqiang Ling Rupasri Mandal Andre Mattman Margaret McKinnon Aspasia Michoulas Daniel Metzger Oluseye A Ogunbayo Bojana Rakic Jacob Rozmus Peter Ruben Bryan Sayson Saikat Santra Kirk R Schultz Kathryn Selby Paul Shekel Sandra Sirrs Cristina Skrypnyk Andrea Superti-Furga Stuart E Turvey Margot I Van Allen David Wishart Jiang Wu John Wu Dimitrios Zafeiriou Leo Kluijtmans Ron A Wevers Patrice Eydoux Anna M Lehman Hilary Vallance Sylvia Stockler-Ipsiroglu Graham Sinclair Wyeth W Wasserman Clara D van Karnebeek

BACKGROUND Whole-exome sequencing has transformed gene discovery and diagnosis in rare diseases. Translation into disease-modifying treatments is challenging, particularly for intellectual developmental disorder. However, the exception is inborn errors of metabolism, since many of these disorders are responsive to therapy that targets pathophysiological features at the molecular or cellular lev...

Journal: :Journal of inborn errors of metabolism and screening 2023

Aromatic L-Amino acid decarboxylase (AADC) deficiency is a rare neurometabolic disorder due to homozygous or compound heterozygous pathogenic variant of the DDC gene, resulting in low synthesis biogenic amines dopamine, serotonin, epinephrine, and norepinephrine. Most patients had severe expression disease with global developmental delay, early hypotonia, movement disorders such as oculogyric c...

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