نتایج جستجو برای: ullrich congenital muscular dystrophy

تعداد نتایج: 169567  

Journal: :Journal of medical genetics 1977
T Furukawa Y Toyokura

Four cases of congenital, hypotonic-sclerotic muscular dystrophy are presented. The patients showed clinically prominent features described by Ullrich, i.e. congenital muscle weakness, hypotonia, and hyperextensibility of distal joints, contractures of proximal joints, high-arched palate, hyperhidrosis, posterior protrusion of calcaneus, and no progression. Muscle biopsies revealed dystrophic c...

Journal: :Proceedings of the National Academy of Sciences of the United States of America 2008
Luciano Merlini Alessia Angelin Tania Tiepolo Paola Braghetta Patrizia Sabatelli Alessandra Zamparelli Alessandra Ferlini Nadir M Maraldi Paolo Bonaldo Paolo Bernardi

Ullrich congenital muscular dystrophy and Bethlem myopathy are skeletal muscle diseases that are due to mutations in the genes encoding collagen VI, an extracellular matrix protein forming a microfibrillar network that is particularly prominent in the endomysium of skeletal muscle. Myoblasts from patients affected by Ullrich congenital muscular dystrophy display functional and ultrastructural m...

Journal: :Neurology India 2009
A Nalini N Gayathri Vani Santosh

BACKGROUND Ullrich congenital muscular dystrophy (UCMD) is a unique congenital disorder characterized clinically by generalized muscle weakness, contractures of the proximal joints and hyperextensibility of the distal joints and begins from birth or early infancy. MATERIALS AND METHODS We prospectively evaluated nine cases of classical UCMD and recorded the clinical phenotypic characteristics...

Journal: :genetics in the 3rd millennium 0
غلامرضا زمانی gholamreza zamani child neurologist, children's medical center, tehran university of medical sciences (tums)

muscular dystrophies are inherited disorders that cause progressive muscle weakness (myopathy) and atrophy (loss of muscle mass) due to defects in one or more genes required for normal muscle function. some of the genes responsible for these conditions have been identified .there are a number of different types of muscular dystrophy. the primary symptom for most types is muscle weakness, althou...

2016
Francesca Sardone Francesco Traina Alice Bondi Luciano Merlini Spartaco Santi Nadir Mario Maraldi Cesare Faldini Patrizia Sabatelli

Collagen VI (COLVI) is a non-fibrillar collagen expressed in skeletal muscle and most connective tissues. Mutations in COLVI genes cause two major clinical forms, Bethlem myopathy and Ullrich congenital muscular dystrophy (UCMD). In addition to congenital muscle weakness, patients affected by COLVI myopathies show axial and proximal joint contractures and distal joint hypermobility, which sugge...

2011
Luciano Merlini Patrizia Sabatelli Annarita Armaroli Saverio Gnudi Alessia Angelin Paolo Grumati Maria Elena Michelini Andrea Franchella Francesca Gualandi Enrico Bertini Nadir Mario Maraldi Alessandra Ferlini Paolo Bonaldo Paolo Bernardi

Six individuals with Ullrich congenital muscular dystrophy (UCMD) and mutations in the genes-encoding collagen VI, aging 5-9, received 3-5 mg/kg of cyclosporine A (CsA) daily for 1 to 3.2 years. The primary outcome measure was the muscle strength evaluated with a myometer and expressed as megalimbs. The megalimbs score showed significant improvement (P = 0.01) in 5 of the 6 patients. Motor func...

2013
Bita BOZORGMEHR Ariana KARIMINEJAD Shahriar NAFISSI Bita JEBELLI Urtizberea ANDONI Corine GARTIOUx Celine LEDEUIL Valérie ALLAMAND Pascale RICHARD Mohammad-Hassan KARIMINEJAD

OBJECTIVE Ullrich congenital muscular dystrophy (UCMD) corresponds to the severe end of the clinical spectrum of neuromuscular disorders caused by mutations in the genes encoding collagen VI (COL VI). We studied four unrelated families with six affected children that had typical UCMD with dominant and recessive inheritance. MATERIALS & METHODS Four unrelated Iranian families with six affected...

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