نتایج جستجو برای: pank2 gene

تعداد نتایج: 1141396  

2014
Peter Johnson Roxanne Melbourne-Chambers Nilesh Desai Emma Greenaway

We present a case of an eleven-year-old boy presenting with progressive extrapyramidal signs and dementia. His imaging findings demonstrated the classic eye-of-the-tiger sign on T2W magnetic resonance imaging. He was diagnosed with pantothenate kinase-associated neurodegeneration (PKAN). This is a rare autosomal recessive inborn error of coenzyme A metabolism, caused by mutations in PANK2. This...

Journal: :Molecular genetics and metabolism 2012
Valerio Leoni Laura Strittmatter Giovanna Zorzi Federica Zibordi Sabrina Dusi Barbara Garavaglia Paola Venco Claudio Caccia Amanda L Souza Amy Deik Clary B Clish Marco Rimoldi Emilio Ciusani Enrico Bertini Nardo Nardocci Vamsi K Mootha Valeria Tiranti

Pantothenate kinase-associated neurodegeneration (PKAN) is a rare, inborn error of metabolism characterized by iron accumulation in the basal ganglia and by the presence of dystonia, dysarthria, and retinal degeneration. Mutations in pantothenate kinase 2 (PANK2), the rate-limiting enzyme in mitochondrial coenzyme A biosynthesis, represent the most common genetic cause of this disorder. How mut...

2013
Chih-Hong Lee Chin-Song Lu Wen-Li Chuang Tu-Hsueh Yeh Shih-Ming Jung Chia-Ling Huang Szu-Chia Lai

OBJECTIVES Pantothenate kinase-associated neurodegeneration (PKAN) is a rare disease caused by pantothenate kinase 2 (PANK2, OMIM 606157) mutations. This study is aimed to investigate clinical presentations, pathologies, and genetics in patients with PKAN. METHODS Two patients with PKAN were reported. We reviewed the literature to include additional 19 patients with PKAN in Eastern Asia. Thes...

2016
Deepak Khatri Daniela Zizioli Natascia Tiso Nicola Facchinello Sara Vezzoli Alessandra Gianoncelli Maurizio Memo Eugenio Monti Giuseppe Borsani Dario Finazzi

Mutations in Pantothenate kinase 2 and Coenzyme A (CoA) synthase (COASY), genes involved in CoA biosynthesis, are associated with rare neurodegenerative disorders with brain iron accumulation. We showed that zebrafish pank2 gene plays an essential role in brain and vasculature development. Now we extended our study to coasy. The gene has high level of sequence identity with the human ortholog a...

Journal: :Genetika 2022

The aim of the study was to analyze genetic basis a various range neurodegenerative disorders manifesting by movement (MD) using next generation sequencing (NGS) clinical exome panel. included total number 42 cases, 36 unrelated and 3 sibling pairs patients diagnosed with disorders, all negative after targeted testing available at Neurology clinic, UCCS, Belgrade, Serbia. In selection responden...

2012
Coro Paisán-Ruiz Abi Li Susanne A. Schneider Janice L. Holton Robert Johnson Desmond Kidd Jeremy Chataway Kailash P. Bhatia Andrew J. Lees John Hardy Tamas Revesz Henry Houlden

The 2 major types of neurodegeneration with brain iron accumulation (NBIA) are the pantothenate kinase type 2 (PANK2)-associated neurodegeneration (PKAN) and NBIA2 or infantile neuroaxonal dystrophy (INAD) due to mutations in the phospholipase A2, group VI (PLA2G6) gene. We have recently demonstrated clinical heterogeneity in patients with mutations in the PLA2G6 gene by identifying a poorly de...

Journal: :Ideggyogyaszati szemle 2010
András Vincze István Kapás Mária J Molnar Gábor G Kovács

Neurodegeneration with brain iron accumulation (NBIA) is a rare, progressive neurodegenerative disorder with extrapyramidal and cognitive clinical symptoms characterized by iron accumulation predominantly in the globus pallidus, cs well as extensive axonal spheroids in various regions of the brain. Recent studies indicate multiple genetic causes, however the illness can occur without obvious ge...

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