نتایج جستجو برای: central hypotonia

تعداد نتایج: 471786  

2016
Melike Ersoy Burak Tatlı Serdar Ceylaner

Zellweger syndrome (ZS) disorders are autosomal recessive peroxisomal biogenesis diseases mainly characterized by neonatal onset severe neurodevelopmental delay, profound hypotonia, craniofacial dysmorphism, hepatic dysfunction, polyneuropathy and loss of hearing and vision. There is a wide genetic heterogeneity that while most ZS disorders are rapidly progressive and incurable, and patients ra...

2014
EMMANOUIL MANOLAKOS ANNALISA VETRO ANTONIOS GARAS LORETTA THOMAIDIS KONSTANTINOS KEFALAS GEORGE KITSOS MONIKA ZIEGLER THOMAS LIEHR ORSETTA ZUFFARDI IOANNIS PAPOULIDIS

Proximal 10q duplication is a well-defined but rare genetic syndrome. Duplication of proximal segments of the long arm of chromosome 10 results in a pattern of malformations, which are distinct from those of the more common distal 10q trisomy syndrome. The present study describes the case of a boy with phenotypic abnormalities (severe central hypotonia, mild ataxia, moderate developmental delay...

2004
Alexis Brice

Keywords Disease names and synonyms Definition/Diagnostic criteria Differential diagnosis Etiology Clinical description Diagnostic methods Epidemiology Management Unresolved questions References Abstract Infantile neuroaxonal dystrophy (INAD) is a rare autosomal recessive neurodegenerative disorder with onset in the first or second year of life. Frequency is unknown. It is characterized by a pr...

2016
Pragashnie Govender Robin W E Joubert

BACKGROUND Clinical assessment of hypotonia is challenging due to the subjective nature of the initial clinical evaluation. This poses dilemmas for practitioners in gaining accuracy, given that the presentation of hypotonia can be either a non-threatening or malevolent sign. The research question posed was how clinical assessment can be improved, given the current contentions expressed in the s...

Journal: :Human molecular genetics 2015
Claire Angebault Majida Charif Naig Guegen Camille Piro-Megy Benedicte Mousson de Camaret Vincent Procaccio Pierre-Olivier Guichet Maxime Hebrard Gael Manes Nicolas Leboucq François Rivier Christian P Hamel Guy Lenaers Agathe Roubertie

Mitochondrial complex I (CI) deficiencies are causing debilitating neurological diseases, among which, the Leber Hereditary Optic Neuropathy and Leigh Syndrome are the most frequent. Here, we describe the first germinal pathogenic mutation in the NDUFA13/GRIM19 gene encoding a CI subunit, in two sisters with early onset hypotonia, dyskinesia and sensorial deficiencies, including a severe optic ...

Journal: :Brain : a journal of neurology 2003
Norma Beatriz Romero Nicole Monnier Louis Viollet Anne Cortey Martine Chevallay Jean Paul Leroy Joël Lunardi Michel Fardeau

We studied seven patients (fetuses/infants) from six unrelated families affected by central core disease (CCD) and presenting with a fetal akinesia syndrome. Two fetuses died before birth (at 31 and 32 weeks) and five infants presented severe symptoms at birth (multiple arthrogryposis, congenital dislocation of the hips, severe hypotonia and hypotrophy, skeletal and feet deformities, kyphoscoli...

Journal: :American journal of human genetics 2017
Manuela Wiessner Andreas Roos Christopher J Munn Ranjith Viswanathan Tamieka Whyte Dan Cox Benedikt Schoser Caroline Sewry Helen Roper Rahul Phadke Chiara Marini Bettolo Rita Barresi Richard Charlton Carsten G Bönnemann Osório Abath Neto Umbertina C Reed Edmar Zanoteli Cristiane Araújo Martins Moreno Birgit Ertl-Wagner Rolf Stucka Christian De Goede Tamiris Borges da Silva Denisa Hathazi Margherita Dell'Aica René P Zahedi Simone Thiele Juliane Müller Helen Kingston Susanna Müller Elizabeth Curtis Maggie C Walter Tim M Strom Volker Straub Kate Bushby Francesco Muntoni Laura E Swan Hanns Lochmüller Jan Senderek

Phosphoinositides are small phospholipids that control diverse cellular downstream signaling events. Their spatial and temporal availability is tightly regulated by a set of specific lipid kinases and phosphatases. Congenital muscular dystrophies are hereditary disorders characterized by hypotonia and weakness from birth with variable eye and central nervous system involvement. In individuals e...

Journal: :American journal of perinatology 2012
Mina Abbassi-Ghanavati James M Alexander Donald D McIntire Rashmin C Savani Kenneth J Leveno

OBJECTIVE Magnesium historically has been used for treatment and/or prevention of eclampsia or preterm labor. More recently, antepartum magnesium sulfate has been suggested for prevention of cerebral palsy in preterm infants. Although adverse effects and toxicity of magnesium in pregnant women are well known, the fetal-neonatal effects of magnesium are less clear. The objective of this study wa...

2010
Ariana Kariminejad Bita Bozorgmehr Alireza Khatami Mohamad-Hasan Kariminejad Cecilia Giunta Beat Steinmann

BACKGROUND The Ehlers-Danlos syndrome type VI (EDSVI) is an autosomal recessive connective tissue disease which is characterized by severe hypotonia at birth, progressive kyphoscoliosis, skin hyperelasticity and fragility, joint hypermobility and (sub-)luxations, microcornea, rupture of arteries and the eye globe, and osteopenia. The enzyme collagen lysyl hydroxylase (LH1) is deficient in these...

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